XVII CONGRESSO MINEIRO DE PNEUMOLOGIA E CIRURGIA TORÁCICA e VI CONGRESSO MINEIRO DE PNEUMOLOGIA PEDIÁTRICA
1º Dia - 10/10/25
2º Dia - 10/11/25
3º Dia - 10/9/25

Roda Viva - Moduladores da CFTR: Nova Era no tratamento da Fibrose Cística Voltar

Regina Terse, Ana Cristina Fernandez e Alberto Vergara

Roda Viva - Moduladores da CFTR: Nova Era no tratamento da Fibrose Cística - Marta Duarte

Artigo Autor(es) Referência
A new era of cystic fibrosis therapy with CFTR modulators. Barros Laura Gomes Boabaid de, Prestes Laura Menestrino, Fernandes Maria Fernanda Gonçalves Meirelles, Silva-Filho Luiz Vicente Ribeiro Ferreira da, Pinto Leonardo Araújo Jornal brasileiro de pneumologia : publicacao oficial da Sociedade Brasileira de Pneumologia e Tisilogia. 2025 Jan; 50(Jan):e20240405. doi: 10.36416/1806-3756/e20240405. pii: S1806-37132024000600500.
Advances in the treatment of cystic fibrosis: CFTR modulators. Pastor-Vivero Maria Dolores, Costa I Colomer Jordi, Martín de Vicente Carlos, Vicente-Santamaria Saioa, Garcia Romero Ruth, González Jiménez David, Luna Paredes Carmen Anales de pediatria. 2025 May; 102(May):503857. doi: 10.1016/j.anpede.2025.503857. pii: S2341-2879(25)00132-2.
CFTR modulator therapy: transforming the landscape of clinical care in cystic fibrosis. Taylor-Cousar Jennifer L, Robinson Paul D, Shteinberg Michal, Downey Damian G Lancet (London, England). 2023 Sep; 402(Sep):1171-1184. doi: 10.1016/S0140-6736(23)01609-4. pii: S0140-6736(23)01609-4.
Cystic Fibrosis Transmembrane Conductance Regulator Modulators in Cystic Fibrosis: A Review of Registry-Based Evidence. Salvatore Donatello, Pepe Angela Journal of clinical medicine. 2025 Jun; 14(Jun):doi: 10.3390/jcm14113978. pii: 3978.
Cystic Fibrosis in the Era of Highly Effective CFTR Modulators. Britto Clemente J, Taylor-Cousar Jennifer L Clinics in chest medicine. 2022 Dec; 43(Dec):xiii-xvi. doi: 10.1016/j.ccm.2022.07.003. pii: S0272-5231(22)00080-6.
Efficacy and Safety of Elexacaftor-Tezacaftor-Ivacaftor in the Treatment of Cystic Fibrosis: A Systematic Review. Kapouni Nikoletta, Moustaki Maria, Douros Konstantinos, Loukou Ioanna Children (Basel, Switzerland). 2023 Mar; 10(Mar):doi: 10.3390/children10030554. pii: 554.
Elexacaftor/tezacaftor/ivacaftor-real-world clinical effectiveness and safety. A single-center Portuguese study. Lopes Kelly, Custódio Catarina, Lopes Carlos, Bolas Raquel, Azevedo Pilar Jornal brasileiro de pneumologia : publicacao oficial da Sociedade Brasileira de Pneumologia e Tisilogia. 2023 ; 49():e20220312. doi: 10.36416/1806-3756/e20220312. pii: e20220312.
Highly effective cystic fibrosis transmembrane conductance (regulator) modulator therapy: shifting the curve for most while leaving some further behind. Chun Stanford W, Somers Maya E, Burgener Elizabeth B Current opinion in pediatrics. 2024 Feb; doi: 10.1097/MOP.0000000000001338. pii: .
Improving outcomes of infections in cystic fibrosis in the era of CFTR modulator therapy. Saiman Lisa Pediatric pulmonology. 2019 Nov; 54 Suppl 3(Nov):S18-S26. doi: 10.1002/ppul.24522. pii: .
Ivacaftor-tezacaftor-elexacaftor, tezacaftor-ivacaftor and lumacaftor-ivacaftor for treating cystic fibrosis: a systematic review and economic evaluation. Edwards Steven J, Farrar Benjamin G, Ennis Kate, Downes Nicole, Wakefield Victoria, Mackenzie Isaac, Walters Archie, Jhita Tracey Health technology assessment (Winchester, England). 2025 May; 29(May):1-111. doi: 10.3310/CPLD8546. pii: .
Long-term therapy with CFTR modulators consistently improves glucose metabolism in adolescents and adults with cystic fibrosis. Cohen Amitay, Mass Alon, Reiter Joel, Zangen David Haim, Cohen-Cymberknoh Malena Respiratory medicine. 2024 Jul; 228(Jul):107664. doi: 10.1016/j.rmed.2024.107664. pii: S0954-6111(24)00138-0.
The clinical effectiveness of elexacaftor/tezacaftor/ivacaftor (ETI) for people with CF without a F508del variant: A systematic review and meta-analysis. Lupas Daniel, Chou Frank Y, Hakani Mohammad Abdullah Al, Kuthiala Ishita, Srikrishnaraj Arjuna, Li Xuan, Potter Naomi, Quon Bradley S Journal of cystic fibrosis : official journal of the European Cystic Fibrosis Society. 2024 Sep; 23(Sep):950-958. doi: 10.1016/j.jcf.2024.07.012. pii: S1569-1993(24)00796-3.
The future of cystic fibrosis treatment: from disease mechanisms to novel therapeutic approaches. Graeber Simon Y, Mall Marcus A Lancet (London, England). 2023 Sep; 402(Sep):1185-1198. doi: 10.1016/S0140-6736(23)01608-2. pii: S0140-6736(23)01608-2.
Nenhuma revista foi definida para este congresso.