XVII CONGRESSO MINEIRO DE PNEUMOLOGIA E CIRURGIA TORÁCICA e VI CONGRESSO MINEIRO DE PNEUMOLOGIA PEDIÁTRICA
1º Dia - 10/10/25
2º Dia - 10/11/25
3º Dia - 10/9/25

Fibrose Cística, Moduladores de CFTR - Onde Estamos? Voltar

Marcelo de Fuccio

Mesa Redonda - Bronquiectasias - Marcelo de Fuccio

Artigo Autor(es) Referência
A new era of cystic fibrosis therapy with CFTR modulators. Barros Laura Gomes Boabaid de, Prestes Laura Menestrino, Fernandes Maria Fernanda Gonçalves Meirelles, Silva-Filho Luiz Vicente Ribeiro Ferreira da, Pinto Leonardo Araújo Jornal brasileiro de pneumologia : publicacao oficial da Sociedade Brasileira de Pneumologia e Tisilogia. 2025 Jan; 50(Jan):e20240405. doi: 10.36416/1806-3756/e20240405. pii: S1806-37132024000600500.
CFTR modulator therapy: transforming the landscape of clinical care in cystic fibrosis. Taylor-Cousar Jennifer L, Robinson Paul D, Shteinberg Michal, Downey Damian G Lancet (London, England). 2023 Sep; 402(Sep):1171-1184. doi: 10.1016/S0140-6736(23)01609-4. pii: S0140-6736(23)01609-4.
CFTR pharmacological modulators: A great advance in cystic fibrosis management. Foucaud P, Mercier J C Archives de pediatrie : organe officiel de la Societe francaise de pediatrie. 2023 Jan; 30(Jan):1-9. doi: 10.1016/j.arcped.2022.11.019. pii: S0929-693X(22)00246-9.
Current state of CFTR modulators for treatment of Cystic Fibrosis. Despotes Katherine A, Donaldson Scott H Current opinion in pharmacology. 2022 08; 65(08):102239. doi: 10.1016/j.coph.2022.102239. pii: S1471-4892(22)00066-2.
Cystic fibrosis transmembrane conductance regulator modulators: Present and future in cystic fibrosis treatment. A review. De la Hoz Diana, Villamil Osorio Milena, Restrepo-Gualteros Sonia M Archivos argentinos de pediatria. 2019 Apr; 117(Apr):e131-e136. doi: 10.5546/aap.2019.eng.e131. pii: .
Discovery and Development of CFTR Modulators for the Treatment of Cystic Fibrosis. Wang Xueqing, Tse Chris, Singh Ashvani Journal of medicinal chemistry. 2025 Jan; doi: 10.1021/acs.jmedchem.4c02547. pii: .
Modulators of CFTR. Updates on clinical development and future directions. Bardin Emmanuelle, Pastor Alexandra, Semeraro Michaela, Golec Anita, Hayes Kate, Chevalier Benoit, Berhal Farouk, Prestat Guillaume, Hinzpeter Alexandre, Gravier-Pelletier Christine, Pranke Iwona, Sermet-Gaudelus Isabelle European journal of medicinal chemistry. 2021 Jan; 213(Jan):113195. doi: 10.1016/j.ejmech.2021.113195. pii: S0223-5234(21)00044-1.
Progress in precision medicine in cystic fibrosis: a focus on CFTR modulator therapy. Tewkesbury Daniel H, Robey Rebecca C, Barry Peter J Breathe (Sheffield, England). 2021 Dec; 17(Dec):210112. doi: 10.1183/20734735.0112-2021. pii: .
Progress of personalized medicine of cystic fibrosis in the times of efficient CFTR modulators. Tümmler Burkhard, Pallenberg Sophia Theres, Dittrich Anna-Maria, Graeber Simon Y, Naehrlich Lutz, Sommerburg Olaf, Mall Marcus A Molecular and cellular pediatrics. 2025 May; 12(May):6. doi: 10.1186/s40348-025-00194-0. pii: .
State of the Art on Approved Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulators and Triple-Combination Therapy. Meoli Aniello, Fainardi Valentina, Deolmi Michela, Chiopris Giulia, Marinelli Francesca, Caminiti Caterina, Esposito Susanna, Pisi Giovanna Pharmaceuticals (Basel, Switzerland). 2021 Sep; 14(Sep):doi: 10.3390/ph14090928. pii: 928.
Nenhuma revista foi definida para este congresso.